<?xml version="1.0" encoding="UTF-8"?><xml><records><record><source-app name="Biblio" version="7.x">Drupal-Biblio</source-app><ref-type>13</ref-type><contributors><authors><author><style face="normal" font="default" size="100%">A Simpson</style></author><author><style face="normal" font="default" size="100%">M. Batech</style></author><author><style face="normal" font="default" size="100%">A. Carmona</style></author><author><style face="normal" font="default" size="100%">S. Lee</style></author><author><style face="normal" font="default" size="100%">A. Poll</style></author><author><style face="normal" font="default" size="100%">S. Edwards</style></author><author><style face="normal" font="default" size="100%">C. Guittari</style></author><author><style face="normal" font="default" size="100%">C. Sutherland</style></author><author><style face="normal" font="default" size="100%">C. Marini-Bettolo</style></author><author><style face="normal" font="default" size="100%">M. Walter</style></author><author><style face="normal" font="default" size="100%">Marlène Jagut</style></author><author><style face="normal" font="default" size="100%">J. Haberlová</style></author><author><style face="normal" font="default" size="100%">V. Hodgkinson</style></author><author><style face="normal" font="default" size="100%">E. Yiu</style></author><author><style face="normal" font="default" size="100%">L. Murphy</style></author><author><style face="normal" font="default" size="100%">TREAT-NMD Global Data systems Oversight Committee (TGDOC)</style></author><author><style face="normal" font="default" size="100%">TREAT-NMD Global Registry Network for SMA</style></author><author><style face="normal" font="default" size="100%">T. Roe</style></author><author><style face="normal" font="default" size="100%">H. Gordish-Dressman</style></author></authors></contributors><titles><title><style face="normal" font="default" size="100%">A retrospective, non-interventional cohort study to compare adults with SMA receiving risdiplamwith untreated patients: Study design.</style></title><secondary-title><style face="normal" font="default" size="100%">4th Scientific International Congress on Spinal Muscular Atrophy</style></secondary-title></titles><keywords><keyword><style  face="normal" font="default" size="100%">/**not applicable**/</style></keyword></keywords><dates><year><style  face="normal" font="default" size="100%">2024</style></year><pub-dates><date><style  face="normal" font="default" size="100%">14/03/2024</style></date></pub-dates></dates><publisher><style face="normal" font="default" size="100%">SMA Europe</style></publisher><pub-location><style face="normal" font="default" size="100%">Ghent, Belgium</style></pub-location><language><style face="normal" font="default" size="100%">eng</style></language><abstract><style face="normal" font="default" size="100%">&lt;p&gt;/**Not applicable**/&lt;/p&gt;
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