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A systematic review of studies that estimated the burden of chronic non-communicable rare diseases using disability-adjusted life years

Publication Type: Peer reviewed scientific article Authors: Claudia Cruz Oliveira; Periklis Charalampous; Julien Delaye; Diana Alecsandra Grad; Pavel Kolkhir; Enkeleint A. Mechili; Brigid Unim; ...

An EU task force to assess the burden of rare diseases

Publication Type: Peer reviewed scientific article Authors: Pavel Kolkhir; Diana Alecsandra Grad; Periklis Charalampous; Claudia Cruz Oliveira; Enkeleint A Mechili; Brigid Unim; David A Pearce; ...

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