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Search results - 4 results
Clinical Evolution and Disease Burden in Belgian Cystic Fibrosis Patients: effect of Newborn Screening?
Publication Type: Peer reviewed scientific article Authors: Noelia Rodriguez Mier; Vermeulen, François; Daneau, G.; Wanyama, S.; Proesmans, Marijke Source: Belgian Journal of Paediatrics, Volume 23, ...
Clinical Evolution and Disease Burden in Belgian Cystic Fibrosis Patients: effect of Newborn Screening?
Publication Type: Peer reviewed scientific article Authors: Noelia Rodriguez Mier; Vermeulen, François; Daneau, G.; Wanyama, S.; Proesmans, Marijke Source: Belgian Journal of Paediatrics, Volume 23, ...
Treatment burden in patients with at least one class IV or V CFTR mutation
Publication Type: Peer reviewed scientific article Authors: Dewulf, Jonas; Vermeulen, François; Simeon Wanyama; Muriel Thomas; Proesmans, Marijke; Dupont, Lieven; De Boeck, Kris Source: Pediatr ...
Is there evidence for correct diagnosis in cystic fibrosis registries?
Publication Type: Peer reviewed scientific article Authors: Muriel Thomas; Lemonnier, Lydie; Gulmans, Vincent; Naehrlich, Lutz; Vermeulen, François; Cuppens, Harry; Castellani, Carlo; Norek, ...